Clinical trial for gene therapy has begun!

This week Audentes Therapeutics has announced that the first patient in the USA has been dosed with AT132. Thus the clinical trial for gene therapy has begun. A very important mile stone has been reached. We are very happy and excited about this. It was worth it that parents world wide did not simply accept … Read more…

Film of the Myotubular Trust with German Subtitles

Here is the great film of the Myotubular Trust with German subtitles. It shows, that sponsoring research for a treatment for centronuclear myopathies in deed pays off. All this the Myotubular Trust made possible with donations! Thank you so much Myotubular Trust and donors! We co-operate closely together with our friends of the Myotubular Trust … Read more…

European Conference

On May 07. and 08., 2016 the European family conference on myotubular myopathy and other centronuclear myopathies takes place in Niedernhausen near Frankfurt, Germany. It is organized together by the Myotubular Trust and ZNM – Zusammen Stark! Information on the conference, the detailed program (incl workshops) and to the registration process you will find here.  … Read more…

Family Conference – Save-the-Date – May 7

  ZNM – Zusammen Stark! e. V. and the Myotubular Trust wil host the next family conference on myotubular myopathy and other centronuclear myopathies on May 07 in Germany near Frankfurt. More information you will find soon on our website: Family conference 2016. We hope that many of you can come!